The new system is the first to use a DNA-mobilizing enzyme called a CRISPR-associated transposase to make targeted gene-sized edits at therapeutically useful levels in human cells.
We are a research organization dedicated to understanding the roots of disease and closing the gap between new biological insights and impact for patients.
By uncovering the biology underlying heart disease, diabetes, cancer, and more, we’re helping to develop effective new treatments that target the root causes of these chronic diseases.
Members of the Data Sciences Platform build open-source technologies that help researchers everywhere connect to the patients, datasets, and tools they need to do life-changing science.
The Spatial Technology Platform expands the impact of spatial -omics through comprehensive support – from study design to data acquisition and processing – for a broad range of users. We also maintain an active research arm that develops and advances cutting edge spatial, imaging, and computational technologies.